They manage to slow down the progression of Huntington's disease using a gene therapy treatment called AMT 130.

An experimental new gene therapy for Huntington’s disease has shown promising results in phase I/II trials, with 75 percent less disease progression observed in the patients receiving the treatment.

Instead of finding treatments for one rare disease, two University at Albany researchers have developed a compound that could ...

For the first time, scientists have successfully treated someone suffering from Huntington's disease, a fatal genetic illness ...

This year saw notable progress in head and neck cancers, Huntington's disease, personalized genetic therapy, and heart ...

On a video call in early September, Sarah Tabrizi first saw the data that she and other researchers studying Huntington’s ...

Gene therapy is becoming a powerful way to treat challenging diseases that don’t respond to traditional treatments, and researchers now report the first success in modifying genes to slow Huntington’s ...

uniQure's AMT-130 receives Breakthrough Therapy designation from FDA for Huntington's disease, based on promising clinical trial data. uniQure N.V. announced that the U.S. FDA has granted Breakthrough ...

This type of medication can help manage the uncontrolled movements that can occur with Huntington’s disease. Huntington’s disease is a neurodegenerative disorder that causes a progressive breakdown of ...

Huntington’s disease (HD) is one of those rare conditions that affects not just the patient but the entire family—medically, emotionally and genetically. This inherited brain disorder causes gradual ...

Huntington’s disease is a brain disorder that can affect various functions, including the ability to swallow — particularly as the disease progresses. Huntington’s disease is a neurogenerative ...

An experimental treatment for the first time slowed the devastating progression of Huntington's disease, gene therapy company uniQure announced Wednesday, a rare hopeful advance against a cruel ...